Hear community perspectives on topics ranging from navigating a diagnosis to reflecting on clinical trial experiences.
Gene therapy is the future of treating rare, genetic diseases that were previously thought to have no cure. CRD is breaking down what gene therapy is and how we are using gene therapy to develop therapies for neuromuscular diseases including Duchenne muscular dystrophy (DMD), limb-girdle muscular dystrophy subtypes, and spinocerebellar ataxia type 3 (SCA3).
Jessica Curran is a DMD mother to her son Conner, CRD board member as well as a DMD patient advocate.