Hear community perspectives on topics ranging from navigating a diagnosis to reflecting on clinical trial experiences.
My husband Keven and I have 3 kids and we’ve been homeschooling for more than 10 years. Here’s a little background of how we got here.
My name is Katie Kuhl and I am a junior in high school right now. I am mostly focused on school and am involved in the math team, DECA, pre-med club, student council, and volunteering at my local animal shelter…
It's National Disability Awareness Month, and what better way to celebrate than by highlighting some amazing TikTok creators who share their stories and journeys of living with a disability.
We are proud to announce the creation of our Scientific Advisory Board (SAB)! Joining the SAB are leading experts in gene therapy and neuromuscular disorders who will help advance our preclinical and clinical development of gene therapy and antisense oligonucleotide programs.