Hear community perspectives on topics ranging from navigating a diagnosis to reflecting on clinical trial experiences.
In the media, people with disabilities often aren’t featured as main characters, if they are included at all, so we wanted to share some kid-friendly shows and movies to help teach kids about acceptance and inclusion. Representation in movies and TV shows is important because it shows people, especially younger kids, that not everyone will look or act the same way and that it is important to be accepting no matter what.
Unlike traditional methods for developing therapeutics for common and (relatively) rare diseases, ultra-rare disease drug development requires a different approach and mechanism in light of a limited ability to commercialize and even reach BLA/NDA approval once clinical trials are complete....
We previously lived in Central California and raised organically fed pork on pasture. When Kal was diagnosed with Duchenne...