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Cornell Employee from Montour Falls to be First to Receive New Therapy for Rare Disorder

Cornell Employee from Montour Falls to be First to Receive New Therapy for Rare Disorder

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Team Led by Monkol Lek Advances Past Pre-IND Phase with DMD Gene Therapy

Team Led by Monkol Lek Advances Past Pre-IND Phase with DMD Gene Therapy

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Recent

Cornell Employee from Montour Falls to be First to Receive New Therapy for Rare Disorder

Terry Horgan, a Cornell graduate and now a Cornell employee, will be the first person in the world to undergo a possible cure for Duchenne muscular dystrophy. Horgan's brother Rich, also a Cornell graduate, is the founder and president of Cure Rare Diseases, the biotech nonprofit behind the treatment.

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Organization Looks To Help Families Impacted By Rare Diseases

Cure Rare Disease, a nonprofit biotechnology research organization, will hold a fundraising event on June 5 in Stamford.

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Hope on the Horizon for Branford Boy, 5, with debilitating, fatal disease

BRANFORD — Max Herzog, 51/2, was a “strapping boy” of almost 11 pounds at birth, so it was a shock for his parents to hear at about 6 months old that he had Duchenne muscular dystrophy, a rare disease that eventually would put him a wheelchair, then take his life.

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Forbes' "30 Under 30" List Highlights the Future Leaders of Biotech

Richard Horgan – 29-year-old Richard Horgan is the founder of Boston-based Cure Rare Disease, a non-profit biotech that develops custom-made drugs for rare diseases, including Duchenne muscular dystrophy. Horgan’s brother Terry is a DMD patient. Cure Rare Disease is currently working on a CRISPR-based therapeutic for this disease. The non-profit has raised about $2.3 million to conduct research on this drug, as well as others in its pipeline.

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Team Led by Monkol Lek Advances Past Pre-IND Phase with DMD Gene Therapy

Duchenne Muscular Dystrophy (DMD) was first documented in the 1860s. More than a hundred years later, researchers discovered the genetic mutation underlying the progressive muscle degeneration that defines this disorder. Despite further studies into the mechanism of DMD, no effective treatment currently exists. Like many rare genetic diseases, DMD ultimately results in loss of quality of life and death. But thanks to advances in gene editing technology, that could soon change.

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Unconventional Life Show: Changing the World One Step at a Time With Cure Rare Disease Founder Rich Horgan

Ep269: Changing the World One Step at a Time, with Cure Rare Disease founder Rich Horgan

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Twitch Streamer, Esports Community Rally Behind Boston Entrepreneur Looking to Rure Brother’s Rare Muscle Condition

The gaming community is getting behind a Boston biotech entrepreneur’s quest to cure his younger brother’s rare genetic muscle condition. For the better part of his adult life, Rich Horgan has been working to fund a customized gene therapy designed specifically for his brother, Terry Horgan, who suffers from Duchenne muscular dystrophy, a rare inherited disease that causes significant muscle degeneration over time — and one that is fatal.

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Rich Horgan Featured as a Business Insider’s 30 Under 40

As the US learned to handle surges in COVID-19 cases that overwhelmed hospitals and shut down cities and confronted systemic racism amid protests sparked by the police killing of George Floyd, healthcare leaders have been navigating a new reality.‍

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The Gamer: Rare Disease Organization Using Fortnite To Raise Money For Charity

An organization devoted to offering treatment to those diagnosed with rare genetic disorders, Cure Rare Disease (CRD), has announced a…

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