This #FactFriday, we’re breaking down the basics of Limb-girdle muscular dystrophy type 2g (LGMD2g) - a progressive, degenerative genetic disease. Cure Rare Disease is dedicated to changing the lives of people with rare diseases through customized therapies.
This #FactFriday, we’re covering Limb-girdle muscular dystrophy type 2I (LGMD2I) - a genetic disease caused by mutations in the FKRP gene that is found throughout the body, and especially in the brain, heart & skeletal muscles. CRD is developing a gene-replacement therapy to treat the condition.
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